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Next generation sequencing as second-tier test in high-throughput newborn screening for nephropathic cystinosis

Nephropathic cystinosis is a rare autosomal recessive lysosomal storage disorder, which causes loss of renal proximal tubular function and progressive loss of glomerular function, finally leading to end stage renal failure at school age. In the course of the disease most patients will need kidney tr...

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Dettagli Bibliografici
Pubblicato in:Eur J Hum Genet
Autori principali: Fleige, Tobias, Burggraf, Siegfried, Czibere, Ludwig, Häring, Julia, Glück, Birgit, Keitel, Lisa Marie, Landt, Olfert, Harms, Erik, Hohenfellner, Katharina, Durner, Jürgen, Röschinger, Wulf, Becker, Marc
Natura: Artigo
Lingua:Inglês
Pubblicazione: Springer International Publishing 2019
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6974606/
https://ncbi.nlm.nih.gov/pubmed/31570786
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41431-019-0521-3
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