Carregant...

Patisiran Pharmacokinetics, Pharmacodynamics, and Exposure‐Response Analyses in the Phase 3 APOLLO Trial in Patients With Hereditary Transthyretin‐Mediated (hATTR) Amyloidosis

Hereditary transthyretin‐mediated (hATTR) amyloidosis is an inherited, rapidly progressive, life‐threatening disease caused by deposition of abnormal transthyretin protein. Patisiran is an RNA interference therapeutic comprising a novel, small interfering ribonucleic acid (ALN‐18328) formulated in a...

Descripció completa

Guardat en:
Dades bibliogràfiques
Publicat a:J Clin Pharmacol
Autors principals: Zhang, Xiaoping, Goel, Varun, Attarwala, Husain, Sweetser, Marianne T., Clausen, Valerie A., Robbie, Gabriel J.
Format: Artigo
Idioma:Inglês
Publicat: John Wiley and Sons Inc. 2019
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6972979/
https://ncbi.nlm.nih.gov/pubmed/31322739
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jcph.1480
Etiquetes: Afegir etiqueta
Sense etiquetes, Sigues el primer a etiquetar aquest registre!