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Patisiran Pharmacokinetics, Pharmacodynamics, and Exposure‐Response Analyses in the Phase 3 APOLLO Trial in Patients With Hereditary Transthyretin‐Mediated (hATTR) Amyloidosis

Hereditary transthyretin‐mediated (hATTR) amyloidosis is an inherited, rapidly progressive, life‐threatening disease caused by deposition of abnormal transthyretin protein. Patisiran is an RNA interference therapeutic comprising a novel, small interfering ribonucleic acid (ALN‐18328) formulated in a...

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Опубликовано в: :J Clin Pharmacol
Главные авторы: Zhang, Xiaoping, Goel, Varun, Attarwala, Husain, Sweetser, Marianne T., Clausen, Valerie A., Robbie, Gabriel J.
Формат: Artigo
Язык:Inglês
Опубликовано: John Wiley and Sons Inc. 2019
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC6972979/
https://ncbi.nlm.nih.gov/pubmed/31322739
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jcph.1480
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