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A Novel AAV-mediated Gene Delivery System Corrects CFTR Function in Pigs
Cystic fibrosis is an autosomal-recessive disease that is caused by a mutant CFTR (cystic fibrosis transmembrane conductance regulator) gene and is characterized by chronic bacterial lung infections and inflammation. Complementation with functional CFTR normalizes anion transport across the airway s...
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| Publicado en: | Am J Respir Cell Mol Biol |
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| Autores principales: | , , , , , , , |
| Formato: | Artigo |
| Lenguaje: | Inglês |
| Publicado: |
American Thoracic Society
2019
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| Materias: | |
| Acceso en línea: | https://ncbi.nlm.nih.gov/pmc/articles/PMC6890402/ https://ncbi.nlm.nih.gov/pubmed/31184507 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1165/rcmb.2019-0006OC |
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