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Sonic Hedgehog repression underlies gigaxonin mutation–induced motor deficits in giant axonal neuropathy

Growing evidence shows that alterations occurring at early developmental stages contribute to symptoms manifested in adulthood in the setting of neurodegenerative diseases. Here, we studied the molecular mechanisms causing giant axonal neuropathy (GAN), a severe neurodegenerative disease due to loss...

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Detaylı Bibliyografya
Yayımlandı:J Clin Invest
Asıl Yazarlar: Arribat, Yoan, Mysiak, Karolina S., Lescouzères, Léa, Boizot, Alexia, Ruiz, Maxime, Rossel, Mireille, Bomont, Pascale
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: American Society for Clinical Investigation 2019
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC6877328/
https://ncbi.nlm.nih.gov/pubmed/31503551
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI129788
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