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Pharmacological analysis of CFTR variants of cystic fibrosis using stem cell-derived organoids

Cystic fibrosis (CF) is a life-shortening genetic disease caused by mutations of CFTR, the gene encoding cystic fibrosis transmembrane conductance regulator. Despite considerable progress in CF therapies, targeting specific CFTR genotypes based on small molecules has been hindered because of the sub...

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Dades bibliogràfiques
Publicat a:Drug Discov Today
Autors principals: Chen, Kevin G., Zhong, Pingyu, Zheng, Wei, Beekman, Jeffrey M.
Format: Artigo
Idioma:Inglês
Publicat: 2019
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6856431/
https://ncbi.nlm.nih.gov/pubmed/31173911
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.drudis.2019.05.029
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