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Therapeutic prospects for Friedreich’s ataxia
Friedreich’s ataxia is a progressive disease affecting multiple organs that is caused by systemic insufficiency of the mitochondrial protein frataxin. Current therapeutic strategies aim to elevate frataxin levels or alleviate consequences of frataxin deficiency. Recent, significant advances within t...
Gorde:
| Argitaratua izan da: | Trends Pharmacol Sci |
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| Egile Nagusiak: | , , |
| Formatua: | Artigo |
| Hizkuntza: | Inglês |
| Argitaratua: |
2019
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| Gaiak: | |
| Sarrera elektronikoa: | https://ncbi.nlm.nih.gov/pmc/articles/PMC6826337/ https://ncbi.nlm.nih.gov/pubmed/30905359 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.tips.2019.02.001 |
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