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Gene Therapy For Beta-Thalassemia: Updated Perspectives

Allogeneic hematopoietic stem cell transplantation was until very recently, the only permanent curative option available for patients suffering from transfusion-dependent beta-thalassemia. Gene therapy, by autologous transplantation of genetically modified hematopoietic stem cells, currently represe...

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Detalles Bibliográficos
Publicado en:Appl Clin Genet
Autores principales: Karponi, Garyfalia, Zogas, Nikolaos
Formato: Artigo
Lenguaje:Inglês
Publicado: Dove 2019
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6765258/
https://ncbi.nlm.nih.gov/pubmed/31576160
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.2147/TACG.S178546
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