Načítá se...

State-of-the-Art 2019 on Gene Therapy for Phenylketonuria

Phenylketonuria (PKU) is considered to be a paradigm for a monogenic metabolic disorder but was never thought to be a primary application for human gene therapy due to established alternative treatment. However, somewhat unanticipated improvement in neuropsychiatric outcome upon long-term treatment...

Celý popis

Uloženo v:
Podrobná bibliografie
Vydáno v:Hum Gene Ther
Hlavní autoři: Grisch-Chan, Hiu Man, Schwank, Gerald, Harding, Cary O., Thöny, Beat
Médium: Artigo
Jazyk:Inglês
Vydáno: Mary Ann Liebert, Inc., publishers 2019
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC6763965/
https://ncbi.nlm.nih.gov/pubmed/31364419
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2019.111
Tagy: Přidat tag
Žádné tagy, Buďte první, kdo otaguje tento záznam!