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High-Throughput Quantification of In Vivo Adeno-Associated Virus Transduction with Barcoded Non-Coding RNAs

Recombinant adeno-associated viruses (rAAVs) have become favorable gene delivery vehicles for expressing therapeutic transgenes. Capsid engineering efforts to produce novel AAVs with improved transduction efficiencies, unique tissue specificities, and reduced host immunities are a direct response to...

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Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Hum Gene Ther
Egile Nagusiak: Xu, Meiyu, Li, Jia, Xie, Jun, He, Ran, Su, Qin, Gao, Guangping, Tai, Phillip W.L.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Mary Ann Liebert, Inc., publishers 2019
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC6703241/
https://ncbi.nlm.nih.gov/pubmed/31072208
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2018.253
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