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Lumacaftor-ivacaftor in the treatment of cystic fibrosis: design, development and place in therapy

Lumacaftor-ivacaftor is a combination of two small molecule therapies targeting the basic defect in cystic fibrosis (CF) at a cellular level. It is a precision medicine and its effects are specific to individuals with two copies of the p.Phe508del gene mutation. The drug combination works by restori...

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Wedi'i Gadw mewn:
Manylion Llyfryddiaeth
Cyhoeddwyd yn:Drug Des Devel Ther
Prif Awdur: Connett, GJ
Fformat: Artigo
Iaith:Inglês
Cyhoeddwyd: Dove 2019
Pynciau:
Mynediad Ar-lein:https://ncbi.nlm.nih.gov/pmc/articles/PMC6650604/
https://ncbi.nlm.nih.gov/pubmed/31409974
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.2147/DDDT.S153719
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