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Lumacaftor-ivacaftor in the treatment of cystic fibrosis: design, development and place in therapy

Lumacaftor-ivacaftor is a combination of two small molecule therapies targeting the basic defect in cystic fibrosis (CF) at a cellular level. It is a precision medicine and its effects are specific to individuals with two copies of the p.Phe508del gene mutation. The drug combination works by restori...

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Enregistré dans:
Détails bibliographiques
Publié dans:Drug Des Devel Ther
Auteur principal: Connett, GJ
Format: Artigo
Langue:Inglês
Publié: Dove 2019
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC6650604/
https://ncbi.nlm.nih.gov/pubmed/31409974
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.2147/DDDT.S153719
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