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Optimized adaptive enrichment designs

Based on a Bayesian decision theoretic approach, we optimize frequentist single- and adaptive two-stage trial designs for the development of targeted therapies, where in addition to an overall population, a pre-defined subgroup is investigated. In such settings, the losses and gains of decisions can...

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Dettagli Bibliografici
Pubblicato in:Stat Methods Med Res
Autori principali: Ondra, Thomas, Jobjörnsson, Sebastian, Beckman, Robert A, Burman, Carl-Fredrik, König, Franz, Stallard, Nigel, Posch, Martin
Natura: Artigo
Lingua:Inglês
Pubblicazione: SAGE Publications 2017
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6613177/
https://ncbi.nlm.nih.gov/pubmed/29254436
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1177/0962280217747312
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