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Development of a patient‐reported outcomes symptom measure for patients with nontransfusion‐dependent thalassemia (NTDT‐PRO(©))

β‐Thalassemia, a hereditary blood disorder caused by reduced or absent synthesis of the β‐globin chain of hemoglobin, is characterized by ineffective erythropoiesis, and can manifest as nontransfusion‐dependent thalassemia (NTDT) or transfusion‐dependent thalassemia (TDT). Many patients with NTDT de...

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Dades bibliogràfiques
Publicat a:Am J Hematol
Autors principals: Taher, Ali, Viprakasit, Vip, Cappellini, Maria Domenica, Sutcharitchan, Pranee, Ward, Richard, Mahmoud, Dalia, Laadem, Abderrahmane, Khan, Anzalee, Gwaltney, Chad, Harding, Gale, Attie, Kenneth, Zhang, Xiaosha, Zou, Jun, Pariseau, Joseph, Hu, X. Henry, Kattamis, Antonis
Format: Artigo
Idioma:Inglês
Publicat: John Wiley & Sons, Inc. 2018
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6587527/
https://ncbi.nlm.nih.gov/pubmed/30394579
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ajh.25343
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