Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction

Antzeko izenburuak

• Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction
  nork: Han, Sang-oh, et al.
  Argitaratua: (2017)
• Enhanced Efficacy from Gene Therapy in Pompe Disease Using Coreceptor Blockade
  nork: Han, Sang-oh, et al.
  Argitaratua: (2015)
• Salmeterol enhances the cardiac response to gene therapy in Pompe disease
  nork: Han, Sang-oh, et al.
  Argitaratua: (2016)
• Synergistic Efficacy from Gene Therapy with Coreceptor Blockade and a β(2)-Agonist in Murine Pompe Disease
  nork: Han, Sang-oh, et al.
  Argitaratua: (2015)
• Progress and challenges of gene therapy for Pompe disease
  nork: Ronzitti, Giuseppe, et al.
  Argitaratua: (2019)