ロード中...

Synergistic Efficacy from Gene Therapy with Coreceptor Blockade and a β(2)-Agonist in Murine Pompe Disease

Pompe disease (glycogen storage disease type II; acid maltase deficiency) is a devastating myopathy resulting from acid α-glucosidase (GAA) deficiency in striated and smooth muscle. Despite the availability of enzyme replacement therapy (ERT) with recombinant human GAA (rhGAA), the limitations of ER...

詳細記述

保存先:
書誌詳細
出版年:Hum Gene Ther
主要な著者: Han, Sang-oh, Li, Songtao, Bird, Andrew, Koeberl, Dwight
フォーマット: Artigo
言語:Inglês
出版事項: Mary Ann Liebert, Inc. 2015
主題:
オンライン・アクセス:https://ncbi.nlm.nih.gov/pmc/articles/PMC4651047/
https://ncbi.nlm.nih.gov/pubmed/26417913
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2015.033
タグ: タグ追加
タグなし, このレコードへの初めてのタグを付けませんか!