載入...
Synergistic Efficacy from Gene Therapy with Coreceptor Blockade and a β(2)-Agonist in Murine Pompe Disease
Pompe disease (glycogen storage disease type II; acid maltase deficiency) is a devastating myopathy resulting from acid α-glucosidase (GAA) deficiency in striated and smooth muscle. Despite the availability of enzyme replacement therapy (ERT) with recombinant human GAA (rhGAA), the limitations of ER...
Na minha lista:
| 發表在: | Hum Gene Ther |
|---|---|
| Main Authors: | , , , |
| 格式: | Artigo |
| 語言: | Inglês |
| 出版: |
Mary Ann Liebert, Inc.
2015
|
| 主題: | |
| 在線閱讀: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4651047/ https://ncbi.nlm.nih.gov/pubmed/26417913 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2015.033 |
| 標簽: |
添加標簽
沒有標簽, 成為第一個標記此記錄!
|