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Desmopressin treatment combined with clotting factor VIII concentrates in patients with non-severe haemophilia A: protocol for a multicentre single-armed trial, the DAVID study

INTRODUCTION: Haemophilia A is an inherited bleeding disorder characterised by factor VIII (FVIII) deficiency. In patients with non-severe haemophilia A, surgery and bleeding are the main indications for treatment with FVIII concentrate. A recent study reported that standard dosing frequently result...

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Publicat a:BMJ Open
Autors principals: Schütte, Lisette M, Cnossen, Marjon H, van Hest, Reinier M, Driessens, Mariette H E, Fijnvandraat, Karin, Polinder, Suzanne, Beckers, Erik A M, Coppens, Michiel, Eikenboom, Jeroen, Laros-van Gorkom, Britta A P, Meijer, Karina, Nieuwenhuizen, Laurens, Mauser-Bunschoten, Evelien P, Leebeek, Frank W G, Mathôt, Ron A A, Kruip, Marieke J H A
Format: Artigo
Idioma:Inglês
Publicat: BMJ Publishing Group 2019
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6500101/
https://ncbi.nlm.nih.gov/pubmed/31015264
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bmjopen-2018-022719
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