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Transcriptome Profiling and Molecular Therapeutic Advances in Cystic Fibrosis: Recent Insights

In cystic fibrosis (CF), mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene disrupt the capacity of the encoded protein to function as a channel to transport chloride ions and water across cell membranes. The consequences are deleterious, system-wide, and immensely vari...

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Detalhes bibliográficos
Publicado no:Genes (Basel)
Main Authors: Ideozu, Justin E., Zhang, Xi, McColley, Susanna, Levy, Hara
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6470978/
https://ncbi.nlm.nih.gov/pubmed/30813620
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/genes10030180
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