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Recent advances in developing therapeutics for cystic fibrosis

Despite hope that a cure was imminent when the causative gene was cloned nearly 30 years ago, cystic fibrosis (CF [MIM: 219700]) remains a life-shortening disease affecting more than 70 000 individuals worldwide. However, within the last 6 years the Food and Drug Administration's approval of Iv...

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Dettagli Bibliografici
Pubblicato in:Hum Mol Genet
Autori principali: Strug, Lisa J, Stephenson, Anne L, Panjwani, Naim, Harris, Ann
Natura: Artigo
Lingua:Inglês
Pubblicazione: Oxford University Press 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6061831/
https://ncbi.nlm.nih.gov/pubmed/30060192
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddy188
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