A carregar...

Vestronidase Alfa: A Review in Mucopolysaccharidosis VII

Mucopolysaccharidosis VII is an extremely rare, autosomal recessive lysosomal storage disorder characterized by a deficiency of β-glucuronidase activity, resulting in partial degradation and accumulation of GAGs in numerous tissues throughout the body, with consequent cellular damage and organ dysfu...

ver descrição completa

Na minha lista:
Detalhes bibliográficos
Publicado no:BioDrugs
Main Authors: McCafferty, Emma H., Scott, Lesley J.
Formato: Artigo
Idioma:Inglês
Publicado em: Springer International Publishing 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6469592/
https://ncbi.nlm.nih.gov/pubmed/30848434
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s40259-019-00344-7
Tags: Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!