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Optimization of a Degradable Polymer-Lipid Nanoparticle for Potent Systemic Delivery of mRNA to the Lung Endothelium and Immune Cells

mRNA therapeutics hold great potential for treating a variety of diseases through protein-replacement, immunomodulation, and gene editing. However, much like siRNA therapy, the majority of progress in mRNA delivery has been confined to the liver. Previously, we demonstrated that poly(β-amino esters)...

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Библиографические подробности
Опубликовано в: :Nano Lett
Главные авторы: Kaczmarek, James C., Kauffman, Kevin J., Fenton, Owen S., Sadtler, Kaitlyn, Patel, Asha K., Heartlein, Michael W., DeRosa, Frank, Anderson, Daniel G.
Формат: Artigo
Язык:Inglês
Опубликовано: 2018
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC6415675/
https://ncbi.nlm.nih.gov/pubmed/30211557
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1021/acs.nanolett.8b02917
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