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Precisely controlling endogenous protein dosage in hPSCs and derivatives to model FOXG1 syndrome

Dosage of key regulators impinge on developmental disorders such as FOXG1 syndrome. Since neither knock-out nor knock-down strategy assures flexible and precise protein abundance control, to study hypomorphic or haploinsufficiency expression remains challenging. We develop a system in human pluripot...

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Publicado en:Nat Commun
Autores principales: Zhu, Wenliang, Zhang, Boya, Li, Mengqi, Mo, Fan, Mi, Tingwei, Wu, Yihui, Teng, Zhaoqian, Zhou, Qi, Li, Wei, Hu, Baoyang
Formato: Artigo
Lenguaje:Inglês
Publicado: Nature Publishing Group UK 2019
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6389984/
https://ncbi.nlm.nih.gov/pubmed/30804331
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41467-019-08841-7
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