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Evaluation of AAV-DJ vector for retinal gene therapy

PURPOSE: The most common virus vector used in gene therapy research for ophthalmologic diseases is the adeno-associated virus (AAV) vector, which has been used successfully in a number of preclinical and clinical studies. It is important to evaluate novel AAV vectors in animal models for application...

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Publicat a:PeerJ
Autors principals: Katada, Yusaku, Kobayashi, Kenta, Tsubota, Kazuo, Kurihara, Toshihide
Format: Artigo
Idioma:Inglês
Publicat: PeerJ Inc. 2019
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6339780/
https://ncbi.nlm.nih.gov/pubmed/30671314
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.7717/peerj.6317
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