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Long-Term Effects of In Vivo Genome Editing in the Mouse Retina Using Campylobacter jejuni Cas9 Expressed via Adeno-Associated Virus

Genome editing with CRISPR systems provides an unprecedented opportunity to modulate cellular responses in pathological conditions by inactivating undruggable targets, such as transcription factors. Previously, we demonstrated that the smallest Cas9 ortholog characterized to date, from Campylobacter...

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Publicado en:Mol Ther
Autores principales: Jo, Dong Hyun, Koo, Taeyoung, Cho, Chang Sik, Kim, Jin Hyoung, Kim, Jin-Soo, Kim, Jeong Hun
Formato: Artigo
Lenguaje:Inglês
Publicado: American Society of Gene & Cell Therapy 2019
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6318782/
https://ncbi.nlm.nih.gov/pubmed/30470629
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymthe.2018.10.009
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