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Shortening the Half-Life of Cas9 Maintains Its Gene Editing Ability and Reduces Neuronal Toxicity

Virus-mediated expression of CRISPR/Cas9 is commonly used for genome editing in animal brains to model or treat neurological diseases, but the potential neurotoxicity of overexpressing bacterial Cas9 in the mammalian brain remains unknown. Through RNA sequencing (RNA-seq) analysis, we find that viru...

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Detalles Bibliográficos
Publicado en:Cell Rep
Autores principales: Yang, Su, Li, Shihua, Li, Xiao-Jiang
Formato: Artigo
Lenguaje:Inglês
Publicado: 2018
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6314484/
https://ncbi.nlm.nih.gov/pubmed/30517854
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.celrep.2018.11.019
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