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Shortening the Half-Life of Cas9 Maintains Its Gene Editing Ability and Reduces Neuronal Toxicity

Virus-mediated expression of CRISPR/Cas9 is commonly used for genome editing in animal brains to model or treat neurological diseases, but the potential neurotoxicity of overexpressing bacterial Cas9 in the mammalian brain remains unknown. Through RNA sequencing (RNA-seq) analysis, we find that viru...

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Detalhes bibliográficos
Publicado no:Cell Rep
Main Authors: Yang, Su, Li, Shihua, Li, Xiao-Jiang
Formato: Artigo
Idioma:Inglês
Publicado em: 2018
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6314484/
https://ncbi.nlm.nih.gov/pubmed/30517854
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.celrep.2018.11.019
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