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ALS mutations of FUS suppress protein translation and disrupt the regulation of nonsense-mediated decay

Amyotrophic lateral sclerosis (ALS) is an incurable neurodegenerative disease characterized by preferential motor neuron death. Approximately 15% of ALS cases are familial, and mutations in the fused in sarcoma (FUS) gene contribute to a subset of familial ALS cases. FUS is a multifunctional protein...

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Dettagli Bibliografici
Pubblicato in:Proc Natl Acad Sci U S A
Autori principali: Kamelgarn, Marisa, Chen, Jing, Kuang, Lisha, Jin, Huan, Kasarskis, Edward J., Zhu, Haining
Natura: Artigo
Lingua:Inglês
Pubblicazione: National Academy of Sciences 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6304956/
https://ncbi.nlm.nih.gov/pubmed/30455313
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.1810413115
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