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Cystic Fibrosis Gene Therapy: Looking Back, Looking Forward

Cystic fibrosis (CF) is an autosomal recessive disease caused by mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene that encodes a cAMP-regulated anion channel. Although CF is a multi-organ system disease, most people with CF die of progressive lung disease that begins...

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Dades bibliogràfiques
Publicat a:Genes (Basel)
Autors principals: Cooney, Ashley L., McCray, Paul B., Sinn, Patrick L.
Format: Artigo
Idioma:Inglês
Publicat: MDPI 2018
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6266271/
https://ncbi.nlm.nih.gov/pubmed/30405068
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/genes9110538
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