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Cystic Fibrosis Gene Therapy: Looking Back, Looking Forward
Cystic fibrosis (CF) is an autosomal recessive disease caused by mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene that encodes a cAMP-regulated anion channel. Although CF is a multi-organ system disease, most people with CF die of progressive lung disease that begins...
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| Опубликовано в: : | Genes (Basel) |
|---|---|
| Главные авторы: | , , |
| Формат: | Artigo |
| Язык: | Inglês |
| Опубликовано: |
MDPI
2018
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| Предметы: | |
| Online-ссылка: | https://ncbi.nlm.nih.gov/pmc/articles/PMC6266271/ https://ncbi.nlm.nih.gov/pubmed/30405068 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/genes9110538 |
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