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Neuraminidase Mediated Desialylation Augments AAV9 Mediated Gene Expression in Skeletal Muscle

BACKGROUND: Following systemic delivery, AAV9-mediated gene expression is significantly increased in ischemic versus non-ischemic muscle, suggesting AAV9 as an attractive vector for treating peripheral arterial disease (PAD). Potential mechanisms underlying ischemia-augmented expression include: 1)...

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Dades bibliogràfiques
Publicat a:J Gene Med
Autors principals: Zhu, Hongling, Wang, Tao, Lye, R. John, French, Brent A., Annex, Brian H.
Format: Artigo
Idioma:Inglês
Publicat: 2018
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6209320/
https://ncbi.nlm.nih.gov/pubmed/30101537
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jgm.3049
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