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Enhancing the Therapeutic Delivery of Oligonucleotides by Chemical Modification and Nanoparticle Encapsulation

Oligonucleotide (ON) drugs, including small interfering RNA (siRNA), microRNA (miRNA) and antisense oligonucleotides, are promising therapeutic agents. However, their low membrane permeability and sensitivity to nucleases present challenges to in vivo delivery. Chemical modifications of the ON offer...

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Publicat a:Molecules
Autors principals: Sun, Yating, Zhao, Yarong, Zhao, Xiuting, Lee, Robert J., Teng, Lesheng, Zhou, Chenguang
Format: Artigo
Idioma:Inglês
Publicat: MDPI 2017
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6158866/
https://ncbi.nlm.nih.gov/pubmed/29027965
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/molecules22101724
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