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Enhancing the Therapeutic Delivery of Oligonucleotides by Chemical Modification and Nanoparticle Encapsulation

Oligonucleotide (ON) drugs, including small interfering RNA (siRNA), microRNA (miRNA) and antisense oligonucleotides, are promising therapeutic agents. However, their low membrane permeability and sensitivity to nucleases present challenges to in vivo delivery. Chemical modifications of the ON offer...

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Publicado en:Molecules
Autores principales: Sun, Yating, Zhao, Yarong, Zhao, Xiuting, Lee, Robert J., Teng, Lesheng, Zhou, Chenguang
Formato: Artigo
Lenguaje:Inglês
Publicado: MDPI 2017
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6158866/
https://ncbi.nlm.nih.gov/pubmed/29027965
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/molecules22101724
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