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Oligonucleotide therapeutics in neurodegenerative diseases

Therapeutics that directly target RNAs are promising for a broad spectrum of disorders, including the neurodegenerative diseases. This is exemplified by the FDA approval of Nusinersen, an antisense oligonucleotide (ASO) therapeutic for spinal muscular atrophy (SMA). RNA targeting therapeutics are cu...

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Detalles Bibliográficos
Publicado en:RNA Biol
Main Authors: Scoles, Daniel R., Pulst, Stefan M.
Formato: Artigo
Idioma:Inglês
Publicado: Taylor & Francis 2018
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6152438/
https://ncbi.nlm.nih.gov/pubmed/29560813
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1080/15476286.2018.1454812
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