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High genetic carrier frequency of Wilson’s disease in France: discrepancies with clinical prevalence

BACKGROUND: Wilson’s disease (WD) is a rare autosomal recessive metabolic disease caused by ATP7B gene mutations tat cause excessively high copper levels, particularly in the liver and brain. The WD phenotype varies in terms of its clinical presentation and intensity. Diagnosing this metabolic disor...

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Detalhes bibliográficos
Publicado no:BMC Med Genet
Main Authors: Collet, Corinne, Laplanche, Jean-Louis, Page, Justine, Morel, Hélène, Woimant, France, Poujois, Aurélia
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2018
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6086069/
https://ncbi.nlm.nih.gov/pubmed/30097039
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12881-018-0660-3
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