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Efficient generation of mouse models of human diseases via ABE- and BE-mediated base editing

A recently developed adenine base editor (ABE) efficiently converts A to G and is potentially useful for clinical applications. However, its precision and efficiency in vivo remains to be addressed. Here we achieve A-to-G conversion in vivo at frequencies up to 100% by microinjection of ABE mRNA tog...

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Detalhes bibliográficos
Publicado no:Nat Commun
Main Authors: Liu, Zhen, Lu, Zongyang, Yang, Guang, Huang, Shisheng, Li, Guanglei, Feng, Songjie, Liu, Yajing, Li, Jianan, Yu, Wenxia, Zhang, Yu, Chen, Jia, Sun, Qiang, Huang, Xingxu
Formato: Artigo
Idioma:Inglês
Publicado em: Nature Publishing Group UK 2018
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6002399/
https://ncbi.nlm.nih.gov/pubmed/29904106
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41467-018-04768-7
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