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High-efficiency transduction of spinal cord motor neurons by intrauterine delivery of integration-deficient lentiviral vectors

Integration-deficient lentiviral vectors (IDLVs) are promising gene delivery tools that retain the high transduction efficiency of standard lentiviral vectors, yet fail to integrate as proviruses and are instead converted into episomal circles. These episomes are metabolically stable and support lon...

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Dettagli Bibliografici
Pubblicato in:J Control Release
Autori principali: Ahmed, Sherif G., Waddington, Simon N., Boza-Morán, Maria Gabriela, Yáñez-Muñoz, Rafael J.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Elsevier Science Publishers 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5845930/
https://ncbi.nlm.nih.gov/pubmed/29289570
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.jconrel.2017.12.029
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