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Effective regeneration of dystrophic muscle using autologous iPSC-derived progenitors with CRISPR-Cas9 mediated precise correction

Duchenne muscular dystrophy (DMD) is a lethal muscle wasting disease caused by a lack of dystrophin, which eventually leads to apoptosis of muscle cells and impaired muscle contractility. Clustered Regularly Interspaced Short Palindromic Repeats/ CRISPR associated protein 9 (CRISPR/Cas9) gene editin...

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Dades bibliogràfiques
Publicat a:Med Hypotheses
Autors principals: Hagan, Mackenzie, Ashraf, Muhammad, Kim, Il-man, Weintraub, Neal L., Tang, Yaoliang
Format: Artigo
Idioma:Inglês
Publicat: 2017
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5793935/
https://ncbi.nlm.nih.gov/pubmed/29317080
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.mehy.2017.11.009
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