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How close are we to therapies for Sanfilippo disease?

Sanfilippo disease is one of mucopolysaccharidoses (MPS), a group of lysosomal storage diseases characterized by accumulation of partially degraded glycosaminoglycans (GAGs). It is classified as MPS type III, though it is caused by four different genetic defects, determining subtypes A, B, C and D....

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Podrobná bibliografie
Vydáno v:Metab Brain Dis
Hlavní autoři: Gaffke, Lidia, Pierzynowska, Karolina, Piotrowska, Ewa, Węgrzyn, Grzegorz
Médium: Artigo
Jazyk:Inglês
Vydáno: Springer US 2017
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC5769821/
https://ncbi.nlm.nih.gov/pubmed/28921412
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s11011-017-0111-4
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