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How close are we to therapies for Sanfilippo disease?

Sanfilippo disease is one of mucopolysaccharidoses (MPS), a group of lysosomal storage diseases characterized by accumulation of partially degraded glycosaminoglycans (GAGs). It is classified as MPS type III, though it is caused by four different genetic defects, determining subtypes A, B, C and D....

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Detalhes bibliográficos
Publicado no:Metab Brain Dis
Main Authors: Gaffke, Lidia, Pierzynowska, Karolina, Piotrowska, Ewa, Węgrzyn, Grzegorz
Formato: Artigo
Idioma:Inglês
Publicado em: Springer US 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5769821/
https://ncbi.nlm.nih.gov/pubmed/28921412
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s11011-017-0111-4
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