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Adding quantitative muscle MRI to the FSHD clinical trial toolbox

OBJECTIVE: To add quantitative muscle MRI to the clinical trial toolbox for facioscapulohumeral muscular dystrophy (FSHD) by correlating it to clinical outcome measures in a large cohort of genetically and clinically well-characterized patients with FSHD comprising the entire clinical spectrum. METH...

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Publicado en:Neurology
Autores principales: Mul, Karlien, Vincenten, Sanne C.C., Voermans, Nicol C., Lemmers, Richard J.L.F., van der Vliet, Patrick J., van der Maarel, Silvère M., Padberg, George W., Horlings, Corinne G.C., van Engelen, Baziel G.M.
Formato: Artigo
Lenguaje:Inglês
Publicado: Lippincott Williams & Wilkins 2017
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC5711504/
https://ncbi.nlm.nih.gov/pubmed/29030457
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0000000000004647
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