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Utility of Genetic Testing for Confirmation of Abnormal Newborn Screening in Disorders of Long-Chain Fatty Acids: A Missed Case of Carnitine Palmitoyltransferase 1A (CPT1A) Deficiency

An 18-month-old male was evaluated after presenting with disproportionately elevated liver transaminases in the setting of acute gastroenteritis. He had marked hepatomegaly on physical exam that was later confirmed with an abdominal ultrasound. Given this clinical picture, suspicion for a fatty acid...

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Dades bibliogràfiques
Publicat a:Int J Neonatal Screen
Autors principals: Dowsett, Leah, Lulis, Lauren, Ficicioglu, Can, Cuddapah, Sanmati
Format: Artigo
Idioma:Inglês
Publicat: 2017
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5523953/
https://ncbi.nlm.nih.gov/pubmed/28748224
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijns3020010
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