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Cobalamin C Disease Missed by Newborn Screening in a Patient with Low Carnitine Level

Cobalamin C (CblC) disease is the most common inherited disorder of intracellular cobalamin metabolism. It is a multisystemic disorder mainly affecting the eye and brain and characterized biochemically by methylmalonic aciduria, low methionine level, and homocystinuria. We report a patient found to...

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Detalhes bibliográficos
Publicado no:JIMD Rep
Main Authors: Ahrens-Nicklas, Rebecca C., Serdaroglu, Esra, Muraresku, Colleen, Ficicioglu, Can
Formato: Artigo
Idioma:Inglês
Publicado em: Springer Berlin Heidelberg 2015
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4484904/
https://ncbi.nlm.nih.gov/pubmed/25772322
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2015_429
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