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Utility of Genetic Testing for Confirmation of Abnormal Newborn Screening in Disorders of Long-Chain Fatty Acids: A Missed Case of Carnitine Palmitoyltransferase 1A (CPT1A) Deficiency

An 18-month-old male was evaluated after presenting with disproportionately elevated liver transaminases in the setting of acute gastroenteritis. He had marked hepatomegaly on physical exam that was later confirmed with an abdominal ultrasound. Given this clinical picture, suspicion for a fatty acid...

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Detaylı Bibliyografya
Yayımlandı:Int J Neonatal Screen
Asıl Yazarlar: Dowsett, Leah, Lulis, Lauren, Ficicioglu, Can, Cuddapah, Sanmati
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: 2017
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC5523953/
https://ncbi.nlm.nih.gov/pubmed/28748224
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijns3020010
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