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Infantile Nephropathic Cystinosis: A Novel CTNS Mutation

Cystinosis is a rare autosomal recessive metabolic disorder characterized by the accumulation of cystine in lysosomes, which results from defects in the carrier-mediated transport protein encoded by the CTNS gene. Infantile nephropathic cystinosis (INC) is one of the major complications of cystinosi...

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Dades bibliogràfiques
Publicat a:Eurasian J Med
Autors principals: Doneray, Hakan, Aldahmesh, Mohammed, Yilmaz, Gulsah, Cinici, Emine, Orbak, Zerrin
Format: Artigo
Idioma:Inglês
Publicat: The Eurasian Journal of Medicine 2017
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5469843/
https://ncbi.nlm.nih.gov/pubmed/28638260
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.5152/eurasianjmed.2017.17039
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