Chargement en cours...

A multi-functional AAV-CRISPR-Cas9 and its host response

CRISPR-Cas9 delivery by AAV holds promise for gene therapy but faces critical barriers due to its potential immunogenicity and limited payload capacity. Here, we demonstrate genome engineering in postnatal mice using AAV-split-Cas9, a multi-functional platform customizable for genome-editing, transc...

Description complète

Enregistré dans:
Détails bibliographiques
Publié dans:Nat Methods
Auteurs principaux: Chew, Wei Leong, Tabebordbar, Mohammadsharif, Cheng, Jason K.W., Mali, Prashant, Wu, Elizabeth Y., Ng, Alex H.M., Zhu, Kexian, Wagers, Amy J., Church, George M.
Format: Artigo
Langue:Inglês
Publié: 2016
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC5374744/
https://ncbi.nlm.nih.gov/pubmed/27595405
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/nmeth.3993
Tags: Ajouter un tag
Pas de tags, Soyez le premier à ajouter un tag!