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Adaptive Immune Response Impairs the Efficacy of Autologous Transplantation of Engineered Stem Cells in Dystrophic Dogs

Duchenne muscular dystrophy is the most common genetic muscular dystrophy. It is caused by mutations in the dystrophin gene, leading to absence of muscular dystrophin and to progressive degeneration of skeletal muscle. We have demonstrated that the exon skipping method safely and efficiently brings...

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Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Mol Ther
Egile Nagusiak: Sitzia, Clementina, Farini, Andrea, Jardim, Luciana, Razini, Paola, Belicchi, Marzia, Cassinelli, Letizia, Villa, Chiara, Erratico, Silvia, Parolini, Daniele, Bella, Pamela, da Silva Bizario, Joao Carlos, Garcia, Luis, Dias-Baruffi, Marcelo, Meregalli, Mirella, Torrente, Yvan
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Nature Publishing Group 2016
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC5154479/
https://ncbi.nlm.nih.gov/pubmed/27506452
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2016.163
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