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Cystic fibrosis – a multiorgan protein misfolding disease

Cystic fibrosis (CF) is a heterogeneous multiorgan disease caused by mutations in the CFTR gene leading to misfolding (and other defects) and consequent dysfunction of CFTR protein. The majority of mutations cause a severe CF phenotype, and people with this condition will require a wide variety of m...

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Dades bibliogràfiques
Publicat a:Future Sci OA
Autors principals: Fraser-Pitt, Douglas, O’Neil, Deborah
Format: Artigo
Idioma:Inglês
Publicat: Future Science Ltd 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5137970/
https://ncbi.nlm.nih.gov/pubmed/28031875
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4155/fso.15.57
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