Murine mucopolysaccharidosis type VII: long term therapeutic effects of enzyme replacement and enzyme replacement followed by bone marrow transplantation.

We demonstrated previously that short term administration of recombinant beta-glucuronidase to newborn mice with mucopolysaccharidosis type VII reduced lysosomal storage in many tissues. Lysosomal storage accumulated gradually after cessation of enzyme replacement therapy. Mice alive at 1 yr of age...

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Dades bibliogràfiques

Publicat a:	J Clin Invest
Autors principals:	Sands, M S, Vogler, C, Torrey, A, Levy, B, Gwynn, B, Grubb, J, Sly, W S, Birkenmeier, E H
Format:	Artigo
Idioma:	Inglês
Publicat:	American Society for Clinical Investigation 1997
Matèries:	Research Article
Accés en línia:	https://ncbi.nlm.nih.govhttps://pmc.ncbi.nlm.nih.gov/articles/PMC507979/ https://ncbi.nlm.nih.govhttps://pubmed.ncbi.nlm.nih.gov/9120003/ https://ncbi.nlm.nih.govhttps://doi.org/10.1172/JCI119322
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