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Reprogramming the Dynamin 2 mRNA by Spliceosome-mediated RNA Trans-splicing
Dynamin 2 (DNM2) is a large GTPase, ubiquitously expressed, involved in membrane trafficking and regulation of actin and microtubule cytoskeletons. DNM2 mutations cause autosomal dominant centronuclear myopathy which is a rare congenital myopathy characterized by skeletal muscle weakness and histopa...
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| Publicat a: | Mol Ther Nucleic Acids |
|---|---|
| Autors principals: | , , , , |
| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
Nature Publishing Group
2016
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| Matèries: | |
| Accés en línia: | https://ncbi.nlm.nih.gov/pmc/articles/PMC5056991/ https://ncbi.nlm.nih.gov/pubmed/27623444 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mtna.2016.67 |
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