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Applications of CRISPR/Cas9 for Gene Editing in Hereditary Movement Disorders
Gene therapy is a potential therapeutic strategy for treating hereditary movement disorders, including hereditary ataxia, dystonia, Huntington’s disease, and Parkinson’s disease. Genome editing is a type of genetic engineering in which DNA is inserted, deleted or replaced in the genome using modifie...
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| Publicado en: | J Mov Disord |
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| Autores principales: | , , |
| Formato: | Artigo |
| Lenguaje: | Inglês |
| Publicado: |
The Korean Movement Disorder Society
2016
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| Materias: | |
| Acceso en línea: | https://ncbi.nlm.nih.gov/pmc/articles/PMC5035944/ https://ncbi.nlm.nih.gov/pubmed/27667185 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.14802/jmd.16029 |
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