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Applications of CRISPR/Cas9 for Gene Editing in Hereditary Movement Disorders

Gene therapy is a potential therapeutic strategy for treating hereditary movement disorders, including hereditary ataxia, dystonia, Huntington’s disease, and Parkinson’s disease. Genome editing is a type of genetic engineering in which DNA is inserted, deleted or replaced in the genome using modifie...

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Detalhes bibliográficos
Publicado no:J Mov Disord
Main Authors: Im, Wooseok, Moon, Jangsup, Kim, Manho
Formato: Artigo
Idioma:Inglês
Publicado em: The Korean Movement Disorder Society 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5035944/
https://ncbi.nlm.nih.gov/pubmed/27667185
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.14802/jmd.16029
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